Gaucher’s disease Pipeline Drugs and Companies Insight Report (2022): Analysis of Clinical Trials, Therapies, Mechanism of Action, Route of Administration, and Developments

Gaucher’s disease Overview

Gaucher disease is a rare, inherited metabolic disorder in which deficiency of the enzyme glucocerebrosidase results in the accumulation of harmful quantities of certain fats (lipids), specifically the glycolipid glucocerebroside, throughout the body especially within the bone marrow, spleen and liver. The symptoms and physical findings associated with Gaucher disease vary greatly from patient to patient.

“Gaucher’s disease Pipeline Insight, 2022″ report by DelveInsight outlines comprehensive insights into the present clinical development scenario and growth prospects across the Gaucher’s disease Market. 

The Gaucher’s disease Pipeline report embraces in-depth commercial and clinical assessment of the pipeline products from the pre-clinical developmental phase to the marketed phase. The report also covers a detailed description of the drug, including the mechanism of action of the drug, clinical studies, NDA approvals (if any), and product development activities comprising the technology, collaborations, mergers acquisition, funding, designations, and other product-related details. 

Some of the key takeaways from the Gaucher’s disease Pipeline Report:

• Companies across the globe are diligently working toward developing novel Gaucher’s disease treatment therapies with a considerable amount of success over the years. Gaucher’s disease Key players such as – Gain therapeutics, M6P Therapeutics, AvroBio, Orphazyme, Eli Lilly and Company, Sanofi, and others, are developing therapies for the Gaucher’s disease treatment 

• Gaucher’s disease Emerging therapies such as – GBA programme, M 011, AVR-RD-02, Arimoclomol, GBA1 Gene Therapy, Venglustat, and others are expected to have a significant impact on the Gaucher’s disease market in the coming years.   
• In April 2022, Sanofi initiated a parallel arm, Phase 3, double-blind, double-dummy,active-comparator, 2 arm study to evaluate the efficacy and safety of daily oral venglustat versus intravenous Cerezyme infusions every two weeks for improvement or stabilization of the neurological manifestations and maintenance of systemic disease stability in participants aged ≥12 and 

Gaucher’s disease Pipeline Therapeutics Assessment

• Gaucher’s disease Assessment by Product Type
• Gaucher’s disease By Stage and Product Type
• Gaucher’s disease Assessment by Route of Administration
• Gaucher’s disease By Stage and Route of Administration
• Gaucher’s disease Assessment by Molecule Type
• Gaucher’s disease by Stage and Molecule Type 

DelveInsight’s Gaucher’s disease Report covers around 16+ products under different phases of clinical development like

• Late-stage products (Phase III)
• Mid-stage products (Phase II)
• Early-stage product (Phase I)
• Pre-clinical and Discovery stage candidates
• Discontinued & Inactive candidates
• Route of Administration 

Emerging Gaucher’s disease Drugs Under Different Phases of Clinical Development Include: 

• GBA programme: Gain therapeutics
• M 011: M6P Therapeutics
• AVR-RD-02: AvroBio
• Arimoclomol: Orphazyme
• GBA1 Gene Therapy: Eli Lilly and Company
• Venglustat: Sanofi 

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Gaucher’s disease Pipeline Analysis:

The Gaucher’s disease pipeline report provides insights into 

• The report provides detailed insights about companies that are developing therapies for the Gaucher’s disease treatment with aggregate therapies developed by each company for the same.
• It accesses the Different therapeutic candidates segmented into early-stage, mid-stage, and late-stage of development for Gaucher’s disease Treatment.
• Gaucher’s disease key companies are involved in targeted therapeutics development with respective active and inactive (dormant or discontinued) projects.
• Gaucher’s disease Drugs under development based on the stage of development, route of administration, target receptor, monotherapy or combination therapy, a different mechanism of action, and molecular type. 
• Detailed analysis of collaborations (company-company collaborations and company-academia collaborations), licensing agreement and financing details for future advancement of the Gaucher’s disease market.

The report is built using data and information traced from the researcher’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations, and featured press releases from company/university websites and industry-specific third-party sources, etc.

Further Gaucher’s disease product details are provided in the report. Download the Gaucher’s disease pipeline report to learn more about the emerging Gaucher’s disease therapies

Gaucher’s disease Pipeline Market Drivers

• Increasing investment for healthcare infrastructure
• Rising prevalence of lysosomal disease

Gaucher’s disease Pipeline Market Barriers

• High cost associated with the treatment
• Lack of awareness among people in developing countries

Scope of Gaucher’s disease Pipeline Drug Insight    

• Coverage: Global
• Key Gaucher’s disease Companies: Gain therapeutics, M6P Therapeutics, AvroBio, Orphazyme, Eli Lilly and Company, Sanofi, and others
• Key Gaucher’s disease Therapies: GBA programme, M 011, AVR-RD-02, Arimoclomol, GBA1 Gene Therapy, Venglustat, and others
• Gaucher’s disease Therapeutic Assessment: Gaucher’s disease current marketed and Gaucher’s disease emerging therapies
• Gaucher’s disease Market Dynamics:  Gaucher’s disease market drivers and Gaucher’s disease market barriers 

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Table of Contents

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